Headache

CGRP Inhibitors

CGRP Inhibitors

CGRP inhibitors are a class of migraine preventive and acute treatments that target calcitonin gene-related peptide (CGRP) or its receptor -- key neuropeptides in migraine pathophysiology -- introduced into clinical practice since 2018.

2026-03-29

At a Glance

CGRP inhibitors (calcitonin gene-related peptide inhibitors) are the first preventive drug class specifically developed for migraine. Monoclonal antibodies (erenumab, fremanezumab, galcanezumab, eptinezumab) reduce monthly headache days by approximately 3.7 to 6.6 days, with 50% or greater response rates of about 40-60%. Oral gepants (ubrogepant, rimegepant) are used for both acute and preventive treatment. They are indicated for patients with episodic migraine (4 or more days per month) or chronic migraine (15 or more days per month).

Definition and Overview

CGRP inhibitors (calcitonin gene-related peptide inhibitors) are a drug class that targets the CGRP signaling pathway, a core pathophysiological mechanism of migraine. CGRP is a potent vasodilatory neuropeptide released from trigeminal nerve terminals, with plasma levels surging during migraine attacks and playing a central role in headache generation.

Erenumab received US FDA approval in 2018, marking the clinical introduction of the first preventive drug class specifically designed for migraine. CGRP inhibitors are broadly divided into monoclonal antibodies (mAbs) and small-molecule gepants.

Etiology and Pathophysiology

During migraine attacks, CGRP is massively released from the trigeminal ganglion and the trigeminovascular complex. CGRP induces meningeal vasodilation, neurogenic inflammation, and central sensitization, resulting in headache, allodynia, and cutaneous sensitivity. CGRP inhibitors prevent migraine and relieve acute symptoms by blocking this pathway.

Symptoms

As CGRP inhibitors are therapeutic agents, there is no specific symptom classification, but understanding the characteristics of their target condition -- migraine -- is important.

Migraine is a primary headache disorder characterized by moderate-to-severe pulsating headache lasting 4 to 72 hours, accompanied by nausea/vomiting, photophobia, and phonophobia. Chronic migraine is defined as headache on 15 or more days per month (with at least 8 days having migraine features).

Diagnosis

Indications for CGRP inhibitors are determined after establishing a migraine diagnosis according to the International Classification of Headache Disorders (ICHD-3) criteria.

  • Episodic migraine: 4 or more monthly headache days, after inadequate response or adverse effects from 1-2 or more prior preventive medications
  • Chronic migraine: headache on 15 or more days per month, after failure of 2 or more prior preventive medications

Treatment

Monoclonal Antibodies (Preventive Treatment)

| Drug | Target | Route | Frequency |
|------|--------|-------|-----------|
| Erenumab | CGRP receptor | Subcutaneous injection | Monthly |
| Galcanezumab | CGRP ligand | Subcutaneous injection | Monthly |
| Fremanezumab | CGRP ligand | Subcutaneous injection | Monthly or quarterly |
| Eptinezumab | CGRP ligand | Intravenous infusion | Quarterly |

Clinical trials demonstrated that monoclonal antibodies reduced monthly headache days by approximately 3.7 to 6.6 days compared to placebo [1][2], with 50% or greater headache reduction response rates of approximately 40-60% [2][4].

Gepants (Small-Molecule CGRP Receptor Antagonists)

  • Ubrogepant: oral acute treatment
  • Rimegepant: approved for both acute and preventive use
  • Atogepant: oral preventive treatment

Unlike triptans, gepants lack vasoconstrictive properties and can be used relatively safely in patients with cardiovascular disease history.

Lasmiditan (Serotonin Receptor Agonist)

Lasmiditan is not a CGRP inhibitor but was introduced in a similar era as an acute migraine treatment that selectively targets the 5-HT1F receptor. Lacking vasoconstrictive effects, it serves as an alternative for patients in whom triptans are contraindicated.

Prognosis

CGRP monoclonal antibodies generally have favorable long-term tolerability. Treatment response is evaluated after a minimum of 3 months of therapy. Approximately one-third of patients respond within 1 to 3 months of treatment initiation, while some require longer periods. Efficacy has been demonstrated even in patients who failed multiple prior preventive medications, making these agents an important option for refractory migraine management.

---

This information is provided for medical educational purposes only and does not replace professional medical advice.
If you are experiencing symptoms, please consult a specialist.
Contact: OSANG Neurosurgery 1599-5453 | osns.co.kr

Frequently Asked Questions

undefined

undefined

undefined

undefined

undefined

undefined

References

  1. [1] Tepper S, Ashina M, Reuter U, Brandes JL, Dolezil D, Silberstein S, et al. (2017). "Safety and efficacy of erenumab for preventive treatment of chronic migraine, a randomised, double-blind, placebo-controlled phase 2 trial." Lancet Neurology, 16: 425-434. PubMed
  2. [2] Goadsby PJ, Reuter U, Hallstrom Y, Broessner G, Bonner JH, Zhang F, et al. (2017). "A controlled trial of erenumab for episodic migraine." New England Journal of Medicine, 377: 2123-2132. PubMed
  3. [3] Dodick DW, Ashina M, Brandes JL, Kudrow D, Lanteri-Minet M, Osipova V, et al. (2018). "ARISE, a phase 3 randomized trial of erenumab for episodic migraine." Cephalalgia, 38: 1026-1037. PubMed
  4. [4] Dodick DW, Silberstein SD, Bigal ME, Yeung PP, Goadsby PJ, Blankenbiller T, et al. (2018). "Effect of fremanezumab compared with placebo for prevention of episodic migraine, a randomized clinical trial." JAMA, 319: 1999-2008. PubMed
CGRP InhibitorsMigraine PreventionErenumabGalcanezumabFremanezumab게판트Chronic Migraine

This content is provided for medical information purposes only and cannot replace professional medical advice. If you have symptoms, please consult a specialist.

Are you concerned about related symptoms?

Get an accurate diagnosis at OSANG Neurosurgery.